VTv Therapeutics Gets FDA Orphan Drug Designation for Sickle Cell Candidate

MT Newswires Live
8 hours ago

VTv Therapeutics (VTVT) said the US Food and Drug Administration granted orphan drug designation to HPPD, its investigational oral treatment for sickle cell disease.

Preclinical studies conducted at Augusta University in a mouse model showed HPPD was well tolerated, increased fetal hemoglobin, and reduced oxidative stress and red blood cell sickling, vTv said Wednesday in a statement.

The treatment increased fetal hemoglobin in a time- and dose-dependent manner, with effects comparable to or exceeding those of hydroxyurea, the company said.

HPPD's safety and efficacy have not been established, and there is no guarantee it will receive regulatory approval or become commercially available, vTv said.

The company's shares rose 2.2% in after-hours trading.

Disclaimer: Investing carries risk. This is not financial advice. The above content should not be regarded as an offer, recommendation, or solicitation on acquiring or disposing of any financial products, any associated discussions, comments, or posts by author or other users should not be considered as such either. It is solely for general information purpose only, which does not consider your own investment objectives, financial situations or needs. TTM assumes no responsibility or warranty for the accuracy and completeness of the information, investors should do their own research and may seek professional advice before investing.

Most Discussed

  1. 1
     
     
     
     
  2. 2
     
     
     
     
  3. 3
     
     
     
     
  4. 4
     
     
     
     
  5. 5
     
     
     
     
  6. 6
     
     
     
     
  7. 7
     
     
     
     
  8. 8
     
     
     
     
  9. 9
     
     
     
     
  10. 10